Agnieszka Waskowska

Efficacy and safety of risdiplam in patients with type 1 spinal muscular atrophy: a 3-year open-label extension of the two-part, phase 2 FIREFISH trial

Maria Mazurkiewicz-Bełdzińska, Maria Mazurkiewicz-Bełdzińska, Laurent Servais, Giovanni Baranello et autres

pl, gb, fr, us, be, ch, it, au, ru, cn, br (code pays fourni par la source)

Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial

Riccardo Masson, Maria Mazurkiewicz-Bełdzińska, Kristy Rose, Laurent Servais et autres

it, pl, au, be, fr, gb, cn, br, us, ch, ru (code pays fourni par la source)

Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial

Eugenio Mercuri, Nicolas Deconinck, Elena Mazzone, A. Nascimento et autres

it, us, be, es, ca, jp, fr, gb, de, pl, ch (code pays fourni par la source)

Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy

Robert C. Sergott, Giulia Maria Amorelli, Giovanni Baranello, Emmanuel Barreau et autres

OBJECTIVE: Evaluation of ophthalmologic safety with focus on retinal safety in patients with spinal muscular atrophy (SMA) treated with risdiplam (EVRYSDI®), a survival of motor neuron 2 splicing modifier associated with retinal toxicity in monkeys. Risdiplam was approved recently for the treatment …

us, it, gb, fr, pl, jp, ch, my (code pays fourni par la source)

Influence of oxygen concentration on T cell proliferation and susceptibility to apoptosis in healthy men and women

Agnieszka Waskowska, Katarzyna A. Lisowska, Agnieszka Daca, Izabella Henc et autres

INTRODUCTION: Much of what we know about the functioning of human T lymphocytes is based on the experiments carried out in atmospheric oxygen (O₂) concentrations, which are significantly higher than those maintained in blood. Interestingly, the gender differences in the activity of …

pl, cz, cy (code pays fourni par la source)