Harichandana Ghanta

Timing is everything: outcomes of allogeneic HSCT in adults with inborn errors of immunity

Katharine Orf, Hannah Al Yousuf, Thomas Andrew Fox, Nadhira Samsudeen et autres

Outcomes following international MDT assessment of adult IEI patients for allogeneic HSCT suggest early referral is vital: patients considered too high risk for transplant have poor outcomes with a 3-year overall survival of 31%.

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National Audit of Long‐Term Real‐World Outcomes of Berotralstat Use in UK Patients With Hereditary Angioedema

Haggar Elbashir, Anthony D. Dorr, Manisha Ahuja, Lorena E. Lorenzo et autres

The data that support the findings of this study are available from the corresponding author upon reasonable request. Appendix S1: all70086-sup-0001-AppendixS1.docx. Please note: The publisher is not responsible for the content or functionality of any supporting information supplied by the authors. Any …

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A multi-centre UK-based survey on angioedema secondary to acquired C1 inhibitor deficiency

Hadeil Morsi, Aarnoud P. Huissoon, Alexandros P. Grammatikos, Andrew Francis Whyte et autres

BACKGROUND: Acquired angioedema due to C1-inhibitor deficiency (AAE-C1-INH) is very rare compared to its prototype, hereditary angioedema. An updated characterization of the AAE-C1-INH cohort in the UK is required to inform management. OBJECTIVES: To describe the disease burden of AAE-C1-INH, long-term prophylaxis …

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Berotralstat for the prophylaxis of hereditary angioedema—Real‐world evidence data from the United Kingdom

Manisha Ahuja, Anthony D. Dorr, Eniola Bode, Anne Pacita Rosillo Boulton et autres

AppendixS1 AppendixS2 Please note: The publisher is not responsible for the content or functionality of any supporting information supplied by the authors. Any queries (other than missing content) should be directed to the corresponding author for the article.

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Berotralstat for the prophylaxis of hereditary angioedema -- Outcomes in the United Kingdom

Manisha Ahuja, Anthony D. Dorr, Eniola Bode, Anne Pacita Rosillo Boulton et autres

gb (code pays fourni par la source)

A Multicentre UK-Based Audit on Acquired C1 Inhibitor Deficiency 2021

Hadeil Morsi, Alexandros P. Grammatikos, Cathal Laurence Steele, Catherine Stroud et autres

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