2026
article
Efficacy and safety of mitapivat in adults with transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial
Maria Domenica Cappellini, Sujit Sheth, Ali Taher, Hanny Al-Samkari, Ali Bulent Antmen, David Benéitez, Giovanna Cannas, Thomas Coates, Lauren Czapla, Jayme L. Dahlin, Jeremie H. Estepp, Elizabeth Feenstra, Пенчо Георгиев, Sarah Gheuens, Gavrielle M. Price, Andreas Glenthøj, Khaled M. Musallam, Kareem Osman, John B. Porter, Hui Shao, Katrin Uhlig, Eduard J. van Beers, Vip Viprakasit, K. H. M. Kuo, Antonis Kattamis, Elena Cassinerio, Diletta Maira, Giovanna Graziadei, Irene Motta, Margherita Migone De Amicis, Natalia Scaramellini, Marianna Romana Giuditta, Giovanni Battista Ferrero, Alessandro Bisaccia, Carmen Maria Gaglioti, Giorgia Mandrile, S. Lauria, Teresa Ceglie, Vincenzo Voi, Raffaella Origa, Anna Rita Denotti, Eleonora Zaccheddu, Susanna Barella, Filomena Longo, E Mari, Olga Sofritti, Francesca Ferrara, Andrea Ricci, Francesca Maria Farina, Domenico Pastore, Annamaria Pasanisi, Maria Pia Solfrizzi, Ahmad Machmouchi, Joseph Klim, Layal Sharrouf, Nathalie Akiki, Suzanne Koussa, Wael Younes, Ahlam Naila Kori, Norhafizatul Aida Amir Khalid, Normala Nordin, Sopian Abdul Wahab, Evelyn Su-Yin Aun, Tze Shin Leong, Lee Ping Chew, Grace Lee Wan Chieng, Xun Ting Tiong, Hong Keng Liew, Chin Hau Wong, Norasmidar Abdul Aziz, Christopher Liam, Soo Min Lim, Азиз Шариф, Yih Seong Wong, Lily Lee Lee Wong, Gilbert Wilfred, Heng Chang Choo, Kishen Sivakumar, Mohd Tarmizi Bin Ahmad Zakhi, Yin Man Lim, Zulaiha Binti Muda, Kogilavani Gunasagaran, Mohamed Najib Bin Unni, Seet Yee Hong, Ai Sim Goh, Carol Chew Yuen Goh, Teng Keat Chew, Su Kien Chieng, Kee Tat Lee, Sui Keat Tan, Veena Selvaratnam, Khaiteri Raghunathan, Kunju Tanusha, Mandy Yap (Yee Yee), Rafizanur Ramli, Syazarin Fidhora Nasution, Eduard van Beers, Cleo Derichs, Joline Saes, Konrad van der Zwet, Anita Rijneveld, Maria Johanna Helma Agnes Kruip, Bart J. Biemond, Erfan Nur, Nawaf Alanazi, Abdulkareem Al Garni, Mohammed Al Shuaibi, Farjah Algahtani, Abdulrahman Al Raizah, Ahmad Alaskar, Ayman Hejazi, Mohsen Alzahrani, Salvador Payán‐Pernía, Eva Mignot Castellano, Margarita Jimenez Jambrina, Marta Morado Arias, Eduardo García Pérez, Miguel Angel Canales Albendea, David Beneitez Pastor, Alba Cabirta Touzón, Alba Puyuelo Benito, Ana Ortuño Cabrera, Ángel Serna Pareja, Cristina García Herce, Inmaculada Fernández Camacho, Marta Hidalgo Soto, Sara Garrido Paniagua, Eduardo José Salido Fiérrez, Almudena Hernández, María José Moreno Belmonte, María Sánchez Villalobos, Raúl Pérez López, Valentín Cabañas Perianes, Shih-Chung Wang, Kuan-Ming Lai, Wei-Hao Wang, Ching-Tien Peng, Min‐Yu Su, Meng‐Yao Lu, Hsiu‐Hao Chang, Peng Shinn-Forng, Shu‐Wei Chou, Ting-Fang Shih, Yung‐Li Yang, Benjapa Khiewvan, Jassada Buaboonnam, Supachai Ekwattanakit, Kittiphong Paiboonsukwong, Saruta Faknuam, Suthat Fucharoen, Adisak Tantiworawit, Chatree Chai‐Adisaksopha, Ekarat Rattarittamrong, Lalita Norasetthada, Pokpong Piriyakhuntorn, Sasinee Hantrakool, Peerapon Wong, Akamon Tapprom, Mayuree Kittijarukhajorn, Piyatida Chumnumsiriwath, Rawisut Deoisares, Noppacharn Uaprasert, Chantiya Chanswangphuwana, Chatphatai Moonla, Ponlapat Rojnuckarin, Suradej Hongeng, Ampaiwan Chuansumrit, Duantida Songdej, Nongnuch Sirachainan, Nattiya Teawtrakul, Chinadol Wanitpongpun, Kanchana Chansung, Pisa Phiphitaporn, Theerin Lanamtieng, Tontanai Numbenjapon, Rattapan Lamool, Yeşim Aydınok, NİHAL KARADAŞ, Şule Ünal Cangül, Fatma Gumruk, Tuncay Hazirolan, Göksel Leblebisatan, Ayse Ozkan, Osman Alphan KÜPESİZ, Funda Tayfun Kupesiz, Mine Erkan, Zeynep Ozturk, Hatice Şaşmaz, Zeynep Karakas, Gülşah Tanyıldız, Serap Karaman, Şifa Şahin, Yasin Yılmaz, Zeynep Nur Aykyol Sari, Khaled Musallam, Ahmad Alrustamani, Biju George, Mojtaba Alhaj, Panayotis Kaloyannidis, D. Mark Layton, Asad Luqmani, Mamta Sohal, Steven Okoli, John Porter, Maciej Garbowski, Perla Eleftheriou, David Kuter, David Smith, Katayoon Goodarzi, Larissa Bornikova, Lorene Pereira, Pamela Hodges, Rachel Rosovsky, Theresa Jundzil, Valerie Wood, John J. Strouse, Nirmish Ramesh Shah, Soheir Adam, Cheryl Mensah, Dorothy Kleinert, May Chien, Claro Lo Chien, Erica Esrick, Jennifer Eile, Ashutosh Lal, Anne Rishon, Madhav Vissa, Kleber Yotsumoto Fertrin, Bart Scott, Lucus Enslin, Michael Linenberger, Nancy Kang, Shreena Portillo, Siobán Keel, Sanjay Shah, Britt Olson, Christine Knoll, Esteban Gomez, Keelin Swartz, Maa‐Ohui Quarmyne, Nicole Mis, Priscila Badia Alonso, Shanna White, Srila Gopal, Annette Von Drygalski, Anthony Nguyen, Stefanie Sacknoff, Farzana Sayani, J. Eric Russell, Scott Peslak, Alexander Glaros, Suzette Meinke, Valérie Babin
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0Institutions déclarées
0Pays d’affiliation déclarés
Résumé indisponible : les résultats de l’étude ne doivent pas être déduits depuis son seul titre.
Contrôle bibliographique ouvert
DOI retrouvé dans Crossref DOI retrouvé ; titre concordant.
- Titre Crossref
- Efficacy and safety of mitapivat in adults with transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial
- Date Crossref
- 01/09/2026
- Éditeur
- Elsevier BV
- Type
- journal-article
Ce recoupement confirme des métadonnées liées au DOI. Il ne confirme ni la méthode ni les conclusions de l’étude et ne compte pas comme une seconde source scientifique indépendante.
Sujets associés
Hemoglobinopathies and Related DisordersBlood transfusion and managementBlood groups and transfusion