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Common variation at 1q23.3, 2p23.3, 2q33.3, and 2p21 influences the risk of acute myeloid leukemia

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63Institutions associées
14Pays d’affiliation

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ABSTRACT: Acute myeloid leukemia (AML) is a complex hematologic malignancy with multiple disease subgroups defined by somatic mutations and heterogeneous outcomes. Although genome-wide association studies (GWAS) have identified a small number of common genetic variants influencing AML risk, the heritable component of this disease outside of familial susceptibility remains largely undefined. Here, we perform a meta-analysis of 4 published GWAS plus 2 new GWAS, totaling 4710 AML cases and 12 938 controls. We identify a new genome-wide significant risk locus for pan-AML at 2p23.3 (rs4665765; P = 1.35 × 10-8; EFR3B, POMC, DNMT3A, and DNAJC27), which also significantly associates with patient survival (P = 6.09 × 10-3). Our analysis also identifies 3 new genome-wide significant risk loci for disease subgroups, including AML with deletions of chromosome 5 and/or 7 at 1q23.3 (rs12078864; P = 7.0 × 10-10; DUSP23) and cytogenetically complex AML at 2q33.3 (rs12988876; P = 3.28 × 10-8; PARD3B) and 2p21 (rs79918355; P = 1.60 × 10-9; EPCAM). We also investigated loci previously associated with the risk of clonal hematopoiesis (CH) or CH of indeterminate potential and identified several variants associated with the risk of AML. Our results further inform on AML etiology and demonstrate the existence of disease subgroup specific risk loci.

Institutions

Newcastle UniversityTaibah UniversityNajran UniversityUniversity of ChicagoTUM KlinikumJohannes Gutenberg University MainzHelmholtz MunichUniversity Medical Center of the Johannes Gutenberg University MainzLudwig-Maximilians-Universität MünchenThe Barbara Ann Karmanos Cancer InstituteRoswell Park Comprehensive Cancer CenterUniversity of South CarolinaNewcastle upon Tyne Hospitals NHS Foundation TrustThe Alfred HospitalUniversity of OxfordBlood Cancer UKSt Thomas' HospitalSt. Thomas HospitalQueen Mary University of LondonUtrecht UniversityUniversity Medical Center UtrechtPrincess Máxima CenterHull York Medical SchoolCancer Research UKUniversity of SouthamptonBirmingham Women's HospitalKing's College LondonLondon CancerNational Center for Tumor DiseasesUniversity Hospital Carl Gustav CarusNationales Centrum für Tumorerkrankungen DresdenCopenhagen University HospitalRigshospitaletOspedale "Santa Maria delle Croci" di RavennaIstituto Oncologico RomagnoloUniversity of BolognaInstituto de Salud Carlos IIIHospital Universitari i Politècnic La FeHôpital PasteurMedical University of GrazUniversity of Rome Tor VergataDélégation Paris 7Institut Universitaire de FranceUniversité Paris CitéCentre Hospitalier Universitaire de LilleLille’s Cardiology HospitalCRUK Lung Cancer Centre of ExcellenceUniversity College LondonSemmelweis UniversityNational Institute of OncologyHeidelberg UniversityUniversity Hospital HeidelbergUniversity Medical Centre MannheimCardiff UniversityUniversity of HelsinkiHelsinki University HospitalMedical University of ViennaThe University of Texas MD Anderson Cancer CenterMunich Leukemia Laboratory (Germany)University of MichiganMichigan MedicineUniversity Hospital Schleswig-HolsteinUniversity of Lübeck

Sujets associés

Acute Myeloid Leukemia ResearchGenomics and Rare DiseasesAcute Lymphoblastic Leukemia research

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